The Parseghian family

In the 18 years since her family began advancing research into the rare, fatal disease that killed three of her four children, Cindy Parseghian has never felt more hopeful about a treatment. Phase One human clinical trials using the drug cyclodextrin to treat Niemann-Pick Type C recently began, the National Institutes of Health confirmed this week.

Comment Policy

We provide this forum for readers to exchange ideas and opinions on the day's news. Passionate views, pointed criticism and critical thinking are welcome. Name-calling, crude language and abuse are not. You must be logged into a personal account on Facebook to comment, FAQ. Readers are responsible for their comments and abuse of this privilege will not be tolerated. We reserve the right, without warning or notification, to remove comments and block users we determine violate our Terms of Service or Comment Rules. Comments reflect the opinions of the author - not those of the Star, StarNet or its parent company.